Long-term Benefit of Sebelipase Alfa Over 96 Weeks in a Diverse Population of Children and Adults With Lysosomal Acid Lipase Deficiency
dc.citation.volume | 66 | |
dc.contributor.author | Burton, Barbara K. | |
dc.contributor.author | Sanchez, Alejandra Consuelo | |
dc.contributor.author | Kostyleva, Maria | |
dc.contributor.author | Allen, Kerstin | |
dc.contributor.author | Friedman, Mark | |
dc.contributor.author | Martins, Ana M. [UNIFESP] | |
dc.coverage | Hoboken | |
dc.date.accessioned | 2020-08-04T13:40:05Z | |
dc.date.available | 2020-08-04T13:40:05Z | |
dc.date.issued | 2017 | |
dc.description.affiliation | Alex Pharmaceut Inc, New Haven, CT USA | |
dc.description.affiliation | Ann & Robert H Lurie Childrens Hosp Chicago, Chicago, IL 60611 USA | |
dc.description.affiliation | Hosp Infantil Mexico Dr Federico Gomez, Mexico City, DF, Mexico | |
dc.description.affiliation | Russian Childrens Clin Hosp, Moscow, Russia | |
dc.description.affiliation | Univ Fed Sao Paulo, Ctr Referencia Erros Inatos Metab, Sao Paulo, Brazil | |
dc.description.affiliationUnifesp | Univ Fed Sao Paulo, Ctr Referencia Erros Inatos Metab, Sao Paulo, Brazil | |
dc.description.source | Web of Science | |
dc.description.sponsorship | Ultragenyx | |
dc.description.sponsorship | ALEXION | |
dc.description.sponsorship | Alexion Pharmaceuticals. Inc. | |
dc.format.extent | 437A-437A | |
dc.identifier | https://doi.org/10.1002/hep.29501 | |
dc.identifier.citation | Hepatology. Hoboken, v. 66, p. 437A-437A, 2017. | |
dc.identifier.doi | 10.1002/hep.29501 | |
dc.identifier.issn | 0270-9139 | |
dc.identifier.uri | https://repositorio.unifesp.br/handle/11600/57281 | |
dc.identifier.wos | WOS:000412089800816 | |
dc.language.iso | eng | |
dc.publisher | Wiley | |
dc.relation.ispartof | Hepatology | |
dc.relation.ispartof | 68th Annual Meeting of the American-Association-for-the-Study-of-Liver-Diseases (AASLD) / Liver Meeting | |
dc.rights | info:eu-repo/semantics/openAccess | |
dc.title | Long-term Benefit of Sebelipase Alfa Over 96 Weeks in a Diverse Population of Children and Adults With Lysosomal Acid Lipase Deficiency | en |
dc.type | info:eu-repo/semantics/conferenceObject |