Early treatment with laronidase improves clinical outcomes in patients with attenuated MPS I: Analysis of eight sibling pairs

Date
2015-02-01
Author
Pleat, Rebecca
Al-Sannaa, Nouriya
Barbouth, Deborah S.
Benhayoun, Youssef
Goizet, Cyril
Guelbert, Norberto
Jones, Simon A.
Kyosen, Sandra [UNIFESP]
Martins, Ana Maria [UNIFESP]
Phornphutkul, Chanika
Reig, Celia
Holder, Iva Ivanovska
Fallet, Shari
Type
Resumo
ISSN
1096-7192
Is part of
Molecular Genetics and Metabolism
DOI
10.1016/j.ymgme.2014.12.208
Metadata
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Citation
Molecular Genetics and Metabolism. San Diego: Academic Press Inc Elsevier Science, v. 114, n. 2, p. S93-S94, 2015.
URI
http://repositorio.unifesp.br/handle/11600/38715
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