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ENCORE: A randomized, controlled, open-label non-inferiority study comparing eliglustat to imiglucerase in Gaucher disease type 1 patients on enzyme replacement therapy who have reached therapeutic goals

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Date
2014-02-01
Author
Cox, Timothy M.
Drelichman, Guillermo
Cravo, Renata
Balwani, Manisha
Burrow, Thomas Andrew
Martins, Ana Maria [UNIFESP]
Lukina, Elena
Rosenbloom, Barry
Ross, Leorah
Angell, Jennifer
Puga, Ana Cristina
Type
Resumo
ISSN
1096-7192
Is part of
Molecular Genetics and Metabolism
DOI
10.1016/j.ymgme.2013.12.061
Metadata
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Citation
Molecular Genetics and Metabolism. San Diego: Academic Press Inc Elsevier Science, v. 111, n. 2, p. S33-S33, 2014.
URI
http://repositorio.unifesp.br/handle/11600/37397
Collections
  • EPM - Outras produções [3595]

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